Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
British singer Jesy Nelson recently took to Instagram to share a devastating update about her 8-month-old twin daughters.
Spinal muscular atrophy is a debilitating genetic condition that’s usually fatal by a few years of age. But an intriguing case study might demonstrate a simple new treatment, with a child showing no ...
Health Secretary was responding to news shared by the former Little Mix star that her twin daughters have been diagnosed with spinal muscular atrophy ...
We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Topline results from a phase 3 clinical trial showed an ...
Treatment with onasemnogene abeparvovec gene therapy for spinal muscular atrophy (SMA) type 1 was associated with less need for nutritional support or nighttime ventilation compared to recommended ...
Jesy Nelson gave birth to her twin girls prematurely in May 2025 - now she's revealed her six-month-olds have been diagnosed with a life-changing illness ...
Credit: Novartis. The approval was supported by data from phase 3 STEER study, which enrolled patients with SMA who were treatment-naive and able to sit but never able to walk independently. Itvisma ...
Jesy Nelson, who gave birth to twins Ocean and Story prematurely in May, said the girls were diagnosed with type 1 spinal muscular atrophy (SMA).
On January 4, former Little Mix singer Jesy Nelson took to Instagram to reveal that her twins have been diagnosed with spinal ...
We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Patients treated with onasemnogene abeparvovec recorded ...
Former Little Mix star Jesy Nelson revealed on social media that her twin girls have been diagnosed with a rare genetic condition called Spinal Muscular Atrophy (SMA) and may never be able to walk.
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